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Psilera is a Florida-based drug discovery company developing non-hallucinogenic psilocybin derivatives and outpatient-compatible psychedelic medicines. Founded in 2019, the female co-founded company has a proprietary compound library of over 1 million novel compounds. Lead candidate PSIL-006 is a non-hallucinogenic psilocybin derivative targeting behavioral variant frontotemporal dementia (bvFTD), with positive preclinical in vivo efficacy data in humanized tau mouse models. Earlier compounds PSIL-001/002 (DMT derivatives) showed improvements in learning and memory.

Development Programmes

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PSIL-006 (Non-Hallucinogenic Psilocybin Derivative)

Psilocybin
Pre-clinical

Non-hallucinogenic psilocybin derivative for behavioral variant frontotemporal dementia (bvFTD). Positive in vivo tau mouse model data (improved sleep, learning, memory). Late IND-enabling with first-in-human targeted 2026. Hesperos organ-on-a-chip collaboration for advanced preclinical modeling.

Programme Tracker

Neurocognitive Disorders

Primary: US (FDA)
Pre-clinicalActive

Late IND-enabling. Company states "poised to advance key assets into the clinic within 12 months" (Jan 2026 CMO appointment PR). Hesperos Human-on-a-Chip collaboration modeling PSIL-006 on patient-derived iPSCs. First-in-human expected 2026.

Milestones

Company milestone

Completed

Actual: Jan 15, 2024

Psilera announces bvFTD as lead indication for PSIL-006 — first psychedelic-derived compound specifically targeting frontotemporal dementia.

Why it matters: bvFTD is a rapidly fatal neurodegenerative disease with no approved treatments. Selecting bvFTD as lead indication signals confidence in the tau-model data and differentiates Psilera from the crowded depression/PTSD space.

Efficacy data

Completed

Actual: Aug 15, 2024

Positive in vivo results in humanized tau mouse model of FTD: PSIL-006 improved sleep patterns, learning, and memory. Positive MTD/safety readouts confirmed. Non-hallucinogenic profile maintained.

Why it matters: First preclinical efficacy signal for a non-hallucinogenic psilocybin derivative in neurodegeneration. Multi-domain improvement (sleep + cognition) suggests broad neuroprotective mechanism beyond isolated endpoints.

Funding milestone

Completed

Actual: Sep 5, 2024

USF Research Foundation invests $200K and publicly endorses PSIL-006 FTD research. Co-founders are USF alumni.

Why it matters: University endorsement and investment validates the science from Psilera's academic origin institution. Provides non-dilutive capital for IND-enabling work.

Company milestone

Completed

Actual: Jan 15, 2025

Psilera hosts first FTD Research Summit in Tampa — convening researchers, academics, and patient advocacy groups (including AFTD) to advance FTD treatment strategies.

Why it matters: KOL engagement and AFTD participation builds the clinical and advocacy network needed for a rare disease program. FTD-specific summit positions Psilera as a thought leader in this therapeutic space.

partnership

Completed

Actual: Feb 20, 2025

Psilera licenses entire DMT patent portfolio to atai Life Sciences (now AtaiBeckley) — upfront payment plus milestones and royalties. Provides Psilera with royalty stream from atai's DMT depression programs (likely VLS-01 for TRD).

Why it matters: Strategic refocus: monetizes legacy DMT IP to fund PSIL-006 FTD development. Creates passive revenue stream from atai's Phase 2 DMT programs without diluting Psilera equity.

Efficacy data

In progress

Actual: Jun 9, 2025

Strategic collaboration with Hesperos Inc. to evaluate PSIL-006 on their Human-on-a-Chip platform — using patient-derived iPSCs in multi-organ microfluidic systems to model PSIL-006 efficacy and safety in neurodegeneration-relevant neural tissues.

Why it matters: Organ-on-a-chip technology provides human-relevant preclinical data beyond rodent models. For a rare disease like bvFTD where patient recruitment is inherently limited, advanced in vitro modeling strengthens the IND package and supports FDA engagement.

Company milestone

Completed

Actual: Jan 8, 2026

Dr. Magali Haas (MD/PhD) appointed CMO. Former Founder/CEO of Cohen Veterans Bioscience; 10+ years at J&J. Company states "poised to advance key assets into the clinic within the next 12 months."

Why it matters: CMO appointment signals imminent IND filing and Phase 1 planning. Haas's experience at Cohen Veterans Bioscience (a leading military mental health research org) and J&J provides the clinical development leadership needed for the transition from preclinical to clinical stage.

Recorded Events

Jan 8, 2026: Company milestone

Jun 9, 2025: Efficacy data

Feb 20, 2025: partnership

Jan 15, 2025: Company milestone

Sep 5, 2024: Funding milestone

Evidence Links

Psilera — PSIL-006 Pipeline Page

company-website - Psilera - Verified

AFTD Coverage of PSIL-006 Data

patient-advocacy - AFTD - Verified

PSIL-025 (Anxiety Neuroplastogen)

Pre-clinical

Non-hallucinogenic psilocybin derivative for anxiety. Early preclinical; no public compound details disclosed. Company focus is on PSIL-006 (bvFTD) and the new AUD neuroplastogen.

AUD Neuroplastogen (NIH/NIAAA-funded)

Psilocybin
Pre-clinical

Novel non-hallucinogenic psilocybin derivative targeting serotonergic (5-HT2A) and glutaminergic pathways affected by AUD. $2M NIH/NIAAA SBIR grant (Oct 2025, 3 years). Passed initial preclinical safety/toxicity. PI: Dr. Jackie von Salm (CSO).

Programme Tracker

Alcohol Use Disorder (AUD)

Primary: US (FDA)
Pre-clinicalActive

NIH/NIAAA SBIR grant-funded IND-enabling studies. Targeting serotonergic and glutaminergic pathways in AUD. Initial preclinical safety and toxicity assessments passed.

Milestones

Funding milestone

Completed

Actual: Oct 3, 2025

Psilera secures $2M NIH/NIAAA SBIR grant (3-year term) to advance novel non-hallucinogenic psilocybin derivative toward IND for alcohol use disorder.

Why it matters: NIH peer-reviewed grant validates the scientific approach and provides 3 years of non-dilutive IND-enabling funding. Expands Psilera's therapeutic scope beyond neurodegeneration into addiction.

Recorded Events

Oct 3, 2025: Funding milestone

Quick Facts

Type
Private Biotech
Founded
2019
Lead Stage
Pre-clinical
Website
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Research Papers

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