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Usona Institute is a US-based 501(c)(3) non-profit medical research organisation (MRO) headquartered in Madison, Wisconsin. Co-founded in 2014 by Bill Linton (CEO of Promega Corporation) and Malynn Utzinger, M.D., Usona was established after Linton witnessed the profound impact of a Johns Hopkins psilocybin study on a terminally ill friend. Unlike commercial drug developers, Usona operates as a mission-driven MRO — conducting and supporting pre-clinical and clinical research on psilocybin and other consciousness-expanding medicines, with the goal of developing accessible, affordable treatments. Its research leadership includes Dr. Charles Raison (Director of Clinical and Translational Research, UW-Madison psychiatrist) and Dr. Alexander Sherwood (medicinal chemist). Usona's psilocybin programme received FDA Breakthrough Therapy Designation for major depressive disorder in 2019. After completing the Phase 2 PSIL201 study (the largest Phase 2 randomised controlled trial of psilocybin for MDD at the time), the Institute launched the Phase 3 uAspire trial in 2024 — a 240-participant, randomised, double-blind, multicentre study comparing 25 mg psilocybin vs placebo in adults with MDD. Usona is also exploring 5-MeO-DMT in early-stage research.

Manufacturing Snapshot

Research-Led (Partner Manufacturing)

Scope & Capabilities

Regulatory / CMC SupportAnalytical / QC Testing

Supply Use Cases

Clinical TrialsResearch Use

GxP / Compliance

General GxP

Facilities & Access

Non-profit research model coordinating investigational drug supply through regulated development pathways.

Manufacturing Details

Supported Substances

Psilocybin investigational supply and quality/CMC coordination in support of clinical trial programs.

Development Programmes

2

Psilocybin (25 mg)

Psilocybin
Phase III

Synthetic psilocybin (25 mg oral, single dose) for major depressive disorder, administered with psychosocial support. FDA Breakthrough Therapy Designation (November 2019). Phase 2 (PSIL201): 104 adults, rapid and sustained antidepressant effect vs active placebo; published JAMA September 2023. Phase 3 uAspire (PSIL301, NCT06308653): ~240 adults, 6-week double-blind + 12-month follow-up. Developed by a non-profit — no commercial pricing pressure.

Programme Tracker

Major Depressive Disorder (MDD)

Primary: US (FDA)
Phase IIIActive

Forecast

nda-submission - Approval eventual: 55%

uAspire (NCT06308653) ongoing — enrolling ~240 adults at US sites including VA. NDA submission targeted 2026 upon Phase 3 completion.

Milestones

Phase II topline

Completed

Actual: Sep 5, 2023

Phase 2 PSIL201 results published in JAMA: single 25 mg psilocybin dose produced rapid, sustained antidepressant effect vs active placebo over 6 weeks (n=104)

Why it matters: JAMA publication provides the strongest evidence base for the Phase 3 programme; high-profile journal validates the clinical approach

Watch next: Phase 3 uAspire enrolment and completion

Phase III started

Completed

Actual: Mar 19, 2024

Phase 3 uAspire study (PSIL301, NCT06308653) launched — ~240 adults, multi-site including VA, 6-week double-blind + 12-month follow-up

Why it matters: Pivotal study required for NDA submission; Usona's non-profit model means results will inform regulatory submissions without commercial licensing barriers

Watch next: Enrollment completion, topline results, NDA submission

Regulatory review accepted

Completed

Actual: Nov 22, 2019

FDA granted BTD to Usona's psilocybin programme for MDD — one of the first psilocybin BTDs granted

Why it matters: BTD provides expedited development pathway and closer FDA collaboration; signals FDA recognition of unmet need in MDD

Watch next: Phase 2 results and Phase 3 launch

Recorded Events

Mar 19, 2024: Phase III started

Sep 5, 2023: Phase II topline

Nov 22, 2019: Regulatory review accepted

Evidence Links

NCT06308653 — uAspire Phase 3 Study (Psilocybin MDD)

trial-registry - ClinicalTrials.gov - Verified

Usona Institute — Drug Development

company-website - Usona Institute - Verified

5-MeO-DMT

5-MeO-DMT
Pre-clinical

Synthetic 5-MeO-DMT (designated MEO201) for a planned Phase 2 efficacy study. GMP drug product manufactured; analytical testing and stability complete. Type B FDA meeting under BTD completed. Phase 2 protocol drafted; facilitator training model developed. Phase 2 initiation targeted mid-2025.

Programme Tracker

Depressive Disorders

Primary: US (FDA)
Pre-clinicalActive

IND-enabling studies complete; Phase 2 initiation targeted mid-2025. Protocol finalized, vendors selected.

Milestones

Pre-clinical completed

Completed

Actual: Dec 1, 2024

GMP manufacturing of 5-MeO-DMT drug product complete; CMC documentation for IND finalized; Type B FDA meeting completed under BTD

Why it matters: IND-enabling package readies Usona for regulatory submission to initiate Phase 2

Watch next: IND submission and Phase 2 first patient dosing

Phase II started

Planned

Likely: Q3 2025

Phase 2 MEO201 study planned for mid-2025 initiation

Why it matters: Would be Usona's second clinical-stage programme; non-profit access model for 5-MeO-DMT distinct from commercial competitors

Watch next: IND submission and first patient dosing announcement

Recorded Events

Dec 1, 2024: Pre-clinical completed

Quick Facts

Type
Non-Profit
Founded
2014
Lead Stage
Phase III
HQ
2800 Woods Hollow Rd., Madison, WI, United States
Website
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Sponsored Trials

5

Collaborated Trials

17